Wyly Wade

Tag: Neurological disorder

Gene therapy reverses Rett Syndrome in Animal Model

Gene therapy in mice shows great success in treating Rett syndrome, a physically disabling form of autism that affects girls. “The treated mice¬†showed profound improvements in motor function, tremors, seizures and compulsive movements” The concept behind gene therapy is simple: deliver a healthy gene to compensate for one that is mutated. New research published today…

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